Sheds Light on the Silent Struggle of Families Battling Huntington’s Disease (Temecula, CA) — In her deeply moving and unflinchingly honest memoir, FALLING ANGELS - A Rhapsody of DNA, and…
HD successfully treated for first time
BBC News reports on early clinical trial results of a gene therapy delivered directly into the brain to lower mutant huntingtin. Patients treated so far show signs of slower disease…
Oxytocin in Huntington’s Disease and ALS-FTD
The journal Frontiers in Molecular Neuroscience spotlights a comprehensive review titled “Oxytocin in Huntington’s disease and the spectrum of amyotrophic lateral sclerosis–frontotemporal dementia” by Bergh et al. The article shares…
May is Huntington’s disease awareness month!
Since 2012, HD-CARE has been supporting research led by Dr. Leslie Thompson at UCI and the UCI HD Clinic. HD-CARE was cofounded by Frances Saldana who lost her three beautiful…
In Memory of Pope Francis, the People’s Pope, and a Friend to the HD Community
Check out Dancing at the Vatican! An inspirational documentary telling the story of a seemingly impossible journey made by families bound by the same devastating, genetically inherited disease, Huntington's. Leaving…
uniQure Announces FDA Breakthrough Therapy Designation Granted to AMT-130 for the Treatment of Huntington’s Disease
Posting from uniQure press releases: April 17, 2025 ~ Breakthrough Therapy designation based on clinical evidence from Phase I/II trials showing meaningful slowing of disease progression ~ ~ Additional regulatory…
Want to learn more about HD?
Make sure to read these articles related to Huntington's disease if you want to learn more! "A Faustian bargain" in the Economist: https://www.economist.com/science-and-technology/2015/03/05/a-faustian-bargain "Is Huntington’s Disease an Unintended Consequence of…
HDF Spotlight Webinar: Launching Hope from the Lab, HD Research Breakthroughs with Dr. Sarah Hernandez
Sarah Hernandez, PhD, at the Hereditary Disease Foundation, discusses clinical trials and recent research for Huntington's disease. A fantastic culmination from hard working scientists around the world. Watch below. https://www.youtube.com/watch?v=wALTraiLmNg
New HD CSF biomarkers informing clinical trials from Dr. Tabrizi Lab
Data from HD-YAS, a deep-phenotyped longitudinal study of young stages 0 and 1 Huntington's disease gene expanded (HDGE) individuals, helps to identify predicted clinical motor diagnosis, and biomarkers of disease…
“A new understanding of Huntington’s disease” – Research from Broad Institute
Scientists at the Broad Institute of MIT and Harvard, Harvard Medical School, and McLean Hospital have discovered a mechanism by which the inherited genetic mutation in Huntington's disease leads to…